{"id":1737,"date":"2018-03-04T18:32:55","date_gmt":"2018-03-05T00:32:55","guid":{"rendered":"https:\/\/restruct-lgmd-2021.pantheonsite.io\/?p=1737"},"modified":"2018-03-04T18:32:55","modified_gmt":"2018-03-05T00:32:55","slug":"1737","status":"publish","type":"post","link":"https:\/\/www.lgmd-info.org\/de\/researcher-interview\/2018\/03\/04\/1737\/","title":{"rendered":"LGMD-FORSCHER: Louise Rodino-Klapac, Ph.D."},"content":{"rendered":"<h2><span style=\"color: #008000;\"><strong>LGMD \"Spotlight-Interview zur Forschung\" <\/strong><\/span><\/h2>\n<p><strong>LGMD-Forscher:<\/strong> Louise Rodino-Klapac, Ph.D.<a href=\"https:\/\/www.lgmd-info.org\/wp-content\/uploads\/2018\/03\/Louise-Rodino-Klapac.png\"><img decoding=\"async\" class=\"lazyload size-medium wp-image-1735 alignright\" src=\"data:image\/svg+xml,%3Csvg%20xmlns%3D%27http%3A%2F%2Fwww.w3.org%2F2000%2Fsvg%27%20width%3D%27300%27%20height%3D%27225%27%20viewBox%3D%270%200%20300%20225%27%3E%3Crect%20width%3D%27300%27%20height%3D%27225%27%20fill-opacity%3D%220%22%2F%3E%3C%2Fsvg%3E\" data-orig-src=\"https:\/\/www.lgmd-info.org\/wp-content\/uploads\/2018\/03\/Louise-Rodino-Klapac-300x225.png\" alt=\"\" width=\"300\" height=\"225\" \/><\/a><\/p>\n<p><strong>Zugeh\u00f6rigkeit:\u00a0 <\/strong>Nationwide Children's Hospital und Myonexus Therapeutics, Inc.<\/p>\n<p><strong>Rolle oder Position<\/strong>: Au\u00dferordentlicher Professor (NCH) und wissenschaftlicher Leiter (Myonexus)<\/p>\n<p>&nbsp;<\/p>\n<p>&nbsp;<\/p>\n<p><strong>Welche Ausbildung haben Sie absolviert, um Ihre derzeitige Position zu erreichen?<\/strong><\/p>\n<p>Ich habe in Molekulargenetik \u00fcber die neuromuskul\u00e4re Entwicklung promoviert.  Anschlie\u00dfend absolvierte ich ein Post-Doc-Stipendium f\u00fcr Gentherapie am Nationalen Kinderkrankenhaus mit Jerry Mendell als meinem Mentor.<\/p>\n<p><strong>Was hat Sie dazu bewogen, eine Karriere in der Forschung und insbesondere in der Erforschung von Muskeldystrophie einzuschlagen?<\/strong><\/p>\n<p>Ich wusste schon in jungen Jahren, dass ich Forscherin werden wollte.  Ich war fasziniert von der Genetik und davon, wie defekte Gene Krankheiten verursachen k\u00f6nnen.  W\u00e4hrend meines Studiums habe ich mich mit der neuromuskul\u00e4ren Entwicklung befasst, und ich war daran interessiert, auf diesem Wissen aufzubauen, um Behandlungen f\u00fcr Muskelkrankheiten zu entwickeln.  Gl\u00fccklicherweise ist die Muskeldystrophie-Forschung ein Schwerpunkt bei Nationwide Children's und bietet mir die M\u00f6glichkeit, meine Ziele zu verwirklichen.<\/p>\n<p><strong>Welche Themen studieren Sie?<\/strong><\/p>\n<p>Ich entwickle gentherapeutische Behandlungen f\u00fcr Gliederg\u00fcrtel- und Duchenne-Muskeldystrophie und bringe diese Behandlungen in klinische Studien ein.  Mein Labor untersucht auch die Krankheitsmechanismen von Gliederg\u00fcrtel-Muskeldystrophien.<\/p>\n<p><strong>Wie wird Ihre Arbeit den Patienten helfen? Ist sie eher wissenschaftlicher Natur oder k\u00f6nnte sie zu einer Behandlung f\u00fcr LGMDs oder MDs im Allgemeinen werden?<\/strong><\/p>\n<p>Unsere Arbeit ist direkt auf Patienten anwendbar.  Wir haben laufende bis bevorstehende klinische Studien f\u00fcr mehrere Formen von LGMD (2B, 2D, 2E) und planen klinische Studien f\u00fcr andere Subtypen.  Wir sind sehr optimistisch, dass der Genersatz eine sinnvolle Behandlung f\u00fcr MD sein wird.<\/p>\n<p><strong>Was w\u00fcrden Sie Patienten und anderen an LGMD Interessierten gerne \u00fcber die Forschung (Ihre eigenen Projekte und \u00fcber das Gebiet im Allgemeinen) mitteilen?<\/strong><\/p>\n<p>Die LGMD-Forschung befindet sich in einer sehr spannenden Phase.  Verbesserungen bei Gentests und Erfolge bei der Gentherapie anderer neuromuskul\u00e4rer Erkrankungen haben die Forschung und die klinischen Versuche f\u00fcr LGMD beschleunigt.  Wir k\u00f6nnen das, was wir bei der Untersuchung einer Form von LGMD gelernt haben, schnell auf eine andere Form \u00fcbertragen.<\/p>\n<p><strong>Was inspiriert Sie, weiterhin in diesem Bereich zu arbeiten? <\/strong><\/p>\n<p>Die Patienten sind meine gr\u00f6\u00dfte Inspiration. Es ist so befriedigend zu wissen, dass all die harte Arbeit, die wir leisten, um Behandlungen in die Klinik zu bringen, den Patienten hoffentlich auf eine sehr sinnvolle Weise zugute kommt!<\/p>\n<p><strong>Wie k\u00f6nnen Patienten Sie ermutigen und Ihre Arbeit unterst\u00fctzen?<\/strong><\/p>\n<p>Geschichten von Patienten zu h\u00f6ren (sowohl Geschichten der Hoffnung als auch der Herausforderungen) ist \u00e4u\u00dferst hilfreich.  Es hilft uns als Forschern, die besonderen Herausforderungen jeder einzelnen Krankheit zu kennen, um die Behandlungen wenn m\u00f6glich anzupassen.  Au\u00dferdem ist es eine st\u00e4ndige Quelle der Motivation, weiter hart zu arbeiten, weil man wei\u00df, dass ein gro\u00dfes Team von Unterst\u00fctzern hinter einem steht!<\/p>","protected":false},"excerpt":{"rendered":"<p>LGMD &#8220;Spotlight Interview on Research\u201d LGMD Researcher: Louise Rodino-Klapac, Ph.D [&hellip;]<\/p>","protected":false},"author":1,"featured_media":1735,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":""},"categories":[91,92],"tags":[],"class_list":["post-1737","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-researcher-interview","category-researcher"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v23.9 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>LGMD RESEARCHER: Louise Rodino-Klapac, Ph.D - LGMD Awareness Foundation<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"http:\/\/www.lgmd-info.org\/de\/researcher-interview\/2018\/03\/04\/1737\/\" \/>\n<meta property=\"og:locale\" content=\"de_DE\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"LGMD RESEARCHER: Louise Rodino-Klapac, Ph.D - 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