LGMD Clinical Trials & Natural History Studies
Clinical Trials and Natural History Studies are vital for advancing research to help find a treatment and cure for LGMD.
ClinicalTrials.gov – This is a searchable registry and results database of federally and privately supported clinical trials conducted in the United States and around the world.
Biotech and Pharmaceutical Companies
Rare Research Map
Following the 2022 Rare Drug Development Symposium, Global Genes released the Rare Disease Roadmap. This toolkit was designed to help advocates, individuals, families, and organizations better understand some of the potential routes to treatment and some of the key concepts that are part of these processes to work with researchers and industry partners throughout the drug development process.
Checklist for Assessing the Legitimacy of Any Proposed LGMD Treatment
Patients can empower themselves by investigating whether or not a treatment has been published and proven to be safe and effective. For the health & safety of the LGMD patient, it is extremely important to determine whether a treatment is legitimate!
5 Question “Checklist” (PDF Document)
Our Advocacy Partners
